The Medical Letter on Drugs and Therapeutics
				
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ISSUE1603
   				ISSUE1603
July 27, 2020
                		
                	Golodirsen (Vyondys 53) for Duchenne Muscular Dystrophy
					
					
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Golodirsen (Vyondys 53) for Duchenne Muscular Dystrophy
July 27, 2020 (Issue: 1603)
					Golodirsen (Vyondys 53 — Sarepta), an antisense
oligonucleotide, has received accelerated approval
from the FDA for treatment of Duchenne muscular
dystrophy (DMD) in the ~8% of patients who have
mutations of the dystrophin gene that are...more
 
        			
        			
						
					
					
					
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